The purpose of this study is to evaluate if the drug GTX-102 is effective with the Angelman population. This is a Phase 3 study, that is a double-blind, sham-controlled study.
Thank you for your interest, but this study is recruiting by invitation only.
United States (Nationwide)
Elizabeth Jalazo
Carolina Institute for Developmental Disabilities
Clinical or Medical
Interventional
Genetics and Genetic Disorders
24-2478