By physician referral or invitation only

A Novel, Regulated Gene Therapy (NGN-401) Study for Female Children with Rett Syndrome

This study will evaluate the safety profile of the investigational gene therapy, NGN-401, in female children with typical Rett syndrome.

Age & Gender

4 years ~ 99 years
Female

Contact the Team

Location

Thank you for your interest, but this study is recruiting by invitation only.

North Carolina (Statewide)

Additional Study Information

Principal Investigator

Yael Shiloh-Malawsky
Neurology-Pediatrics

Study Type

Clinical or Medical
Interventional

Study Topics

Brain, Head, Nervous System

IRB Number

25-0609

ClinicalTrials.gov

NCT05898620

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